Changing the lives of patients with inherited diseases

VP-001 - Retinitis Pigmentosa Type 11 (RP11)

RP is a severe and progressive blinding eye disease that begins in childhood. VP-001 is a first-in-class and potentially disease-modifying drug to treat RP11.

PYC-001 - Autosomal Dominant Optic Atrophy (ADOA)

ADOA is a progressive and irreversible blinding eye disease for which there are currently no available treatments. PYC-001 is a potentially disease-modifying drug to treat the underlying cause of ADOA.

PYC-002 - Phelan McDermid Syndrome (PMS)

PMS is a severe nuerodevelopmental disorder that can cause a wide range of medical, intellectual and behavioural challenges.

There are no available therapies for patients with PMS. PYC-002 seeks to address the underlying cause of PMS.

PYC-003 - Autosomal Dominant Polycystic Kidney Disease

ADPKD is a severe disorder that causes cysts to form in a patients kidneys which can ultimately lead to the patient requiring a kidney transplant.
There are no available therapies for patients with ADPKD that address the underlying cause of the disease.